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Health policy
Original research
Global insight into rare disease and orphan drug definitions: a systematic literature review

Authors

  • Ghada Mohammed Abozaid Centre for Public Health, Institute of Clinical Sciences B, Royal Victoria Hospital, Queen's University Belfast School of Medicine, Dentistry and Biomedical Sciences, Belfast, UKPharmacy Practice, Princess Nourah bint Abdulrahman University, Riyadh, Saudi Arabia PubMed articlesGoogle scholar articles
  • Katie Kerr Centre for Public Health, Institute of Clinical Sciences B, Royal Victoria Hospital, Queen's University Belfast School of Medicine, Dentistry and Biomedical Sciences, Belfast, UK PubMed articlesGoogle scholar articles
  • Hiba Alomary Department of Applied Linguistics, Princess Nourah bint Abdulrahman University, Riyadh, Saudi Arabia PubMed articlesGoogle scholar articles
  • Hussain A Al-Omar Department of Clinical Pharmacy, College of Pharmacy, King Saud University, Riyadh, Saudi Arabia PubMed articlesGoogle scholar articles
  • Amy McKnight Centre for Public Health, Institute of Clinical Sciences B, Royal Victoria Hospital, Queen's University Belfast School of Medicine, Dentistry and Biomedical Sciences, Belfast, UK PubMed articlesGoogle scholar articles
  1. Correspondence to Dr Ghada Mohammed Abozaid; gabozaid01{at}qub.ac.uk
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Citation

Abozaid GM, Kerr K, Alomary H, et al
Global insight into rare disease and orphan drug definitions: a systematic literature review
BMJ Open 2025;15:e086527. doi: 10.1136/bmjopen-2024-086527

Publication history

  • Received March 16, 2024
  • Accepted December 23, 2024
  • First published January 25, 2025.
Online issue publication 
January 25, 2025
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© Author(s) (or their employer(s)) 2025. Re-use permitted under CC BY. Published by BMJ Group. https://creativecommons.org/licenses/by/4.0/This is an open access article distributed in accordance with the Creative Commons Attribution 4.0 Unported (CC BY 4.0) license, which permits others to copy, redistribute, remix, transform and build upon this work for any purpose, provided the original work is properly cited, a link to the licence is given, and indication of whether changes were made. See: https://creativecommons.org/licenses/by/4.0/.